2D Animation of Intrathecal Drug Delivery for SMA
A 2D animation shows how drugs for SMA may be delivered to the central nervous system via intrathecal infusion into the spinal cord.
Spinal muscular atrophy, SMA, RNA, mRNA, splicing, gene, genetic, DNA, antisense, motor neuron, splice, Therapy, Intrathecal, delivery, drug, mechanism, central nervous system, spinal cord, epidural, inject, needle, cerebrospinal fluid, blood-brain barrier, vertebra, axon, dendrite
- ID: 16952
- Source: DNALC.SMA
Dr. Sumner explains how drugs can be delivered into the central nervous system.
An animation shows how antisense oligonucleotide therapy for SMA utilizes RNA splicing.
Dr. Sumner discusses the clinical trial process for SMA antisense oligonucleotide therapy.
An animation shows alternate splicing of the SMN2 gene.
An animation introduces DNA and the pattern of inheritance for SMA.
A step-by-step 2D animation shows the details of RNA splicing.
Dr. De Vivo provides an overview of SMA, and describes the four SMA types.
Frank, an SMA parent, describes the genetics of SMA.
Drs. Sharp and Sumner describe how RNA splicing can be used as a therapy for SMA.
Dr. Sumner describes small molecule therapies for SMA.